A Long Term Safety Study of BCX9930 in Subjects With Paroxysmal Nocturnal Hemoglobinuria (PNH)
Status:
Enrolling by invitation
Trial end date:
2025-01-01
Target enrollment:
Participant gender:
Summary
This study is designed to evaluate the long-term safety of daily oral treatment with BCX9930
in subjects who have participated in a previous BCX9930 trial for PNH and showed a benefit of
treatment as determined by the Investigator. The study allows continued access to BCX9930 for
enrolled subjects. The study will also evaluate the long-term effectiveness and impact on
quality of life and general well-being of BCX9930 treatment, and the subject's satisfaction
with the medication.