A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease
Status:
Terminated
Trial end date:
2014-12-01
Target enrollment:
Participant gender:
Summary
The objective of this study was to evaluate the efficacy and safety of treatment with 4000
litre (L) alglucosidase alfa (Lumizyme®) in Pompe participants.