Application of Miglustat in Patients With Niemann-Pick Type C

• Status: Completed
• Trial end date: 2010-12-01
• Target enrollment: 0
• Participant gender: All

Summary

To evaluate the changes in cognitive function after miglustat treatment in Niemann-Pick type C patients.

• Phase: Phase 3
• Accepts Healthy Volunteers?: No

Details

• Lead Sponsor: National Taiwan University Hospital
• Treatments: 1-Deoxynojirimycin; Miglustat

Criteria

Inclusion Criteria:

• Confirm diagnosis of Niemann-Pick C disease

• Symptomatic including motor or mental symptoms

Exclusion Criteria:

• Unknown severe diarrhea for more than 7 day

• Allergy to miglustat