Overview

BSEP Function Rescue During Childhood Inhereditary Cholestatic Diseases

Status:
Not yet recruiting
Trial end date:
2023-12-30
Target enrollment:
Participant gender:
Summary
The purpose of the study is to improve the prognosis of inhereditary cholestasis caused by ABCB11 gene mutations by using BSEP function rescue drugs
Phase:
Phase 2/Phase 3
Details
Lead Sponsor:
Children's Hospital of Fudan University
Treatments:
4-phenylbutyric acid