Clinical Curative Effect Evaluation Study of Treatment of Oral Deferiprone Tablets in Aceruloplasminaemia Patients
Status:
Recruiting
Trial end date:
2021-11-23
Target enrollment:
Participant gender:
Summary
Aceruloplasminemia is an autosomal recessive disorder characterized by iron deposition in the
brain and visceral organs. Deferiprone was used to treat aceruloplasminemia in previous
study. In this study, we will assess the clinical curative effect evaluation of oral
deferiprone in Chinese aceruloplasminemia patients.
Phase:
Early Phase 1
Details
Lead Sponsor:
First Affiliated Hospital of Fujian Medical University