Overview

Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation

Status:
Recruiting
Trial end date:
2022-02-01
Target enrollment:
Participant gender:
Summary
In this study, the investigators test 2 dose levels of thiotepa (5 mg/kg and 10 mg/kg) added to the backbone of targeted reduced dose IV busulfan, fludarabine and rabbit anti-thymocyte globulin (rATG) to determine the minimum effective dose required for reliable engraftment for subjects undergoing hematopoietic stem cell transplantation for non-malignant disease.
Phase:
Phase 1/Phase 2
Details
Lead Sponsor:
University of Florida
Collaborator:
Live Like Bella Pediatric Cancer Research
Treatments:
Antilymphocyte Serum
Busulfan
Fludarabine
Fludarabine phosphate
Thiotepa
Thymoglobulin