Effect of Glycerol Trierucate on Clinical Course of Adrenoleukodystrophy
Status:
Terminated
Trial end date:
2014-12-01
Target enrollment:
Participant gender:
Summary
OBJECTIVES: I. Evaluate the clinical efficacy of combination glyceryl trierucate and glyceryl
trioleate (Lorenzo's Oil) therapy in boys with X-linked adrenoleukodystrophy.
II. Compare the frequency and severity of neurological disability of study patients with
untreated historical controls.
Phase:
Phase 2
Details
Lead Sponsor:
Hugo W. Moser Research Institute at Kennedy Krieger, Inc.