Overview

Efficacy and Safety of Imatinib in Scleroderma

Status:
Completed
Trial end date:
2010-12-01
Target enrollment:
Participant gender:
Summary
In vitro studies have shown that imatinib 1mM inhibits strongly the growth of cutaneous fibroblasts. The hypothesis is that imatinib inhibits PDGFR which is known to be a potential target for the molecule, as recently also proposed after the discovery of autoantibodies activating the PDGF receptors. Recent data indicate that TGFb is also a potential target of imatinib. Cutaneous scleroderma is characterized by progressive cutaneous fibrosis caused by hyperactive dermal fibroblasts. Since no established treatment for skin sclerosis in scleroderma is currently available. This study will test the safety and efficacy of imatinib in the treatment of patients with scleroderma and severe cutaneous involvement.
Phase:
Phase 2
Details
Lead Sponsor:
University Hospital, Bordeaux
Collaborators:
Ministry of Health, France
Novartis
Treatments:
Imatinib Mesylate