Overview

Efficacy and Safety of Rapamycin Versus Vigabatrin in the Prevention of Tuberous Sclerosis Complex Symptoms in Infants

Status:
Recruiting
Trial end date:
2026-03-01
Target enrollment:
Participant gender:
Summary
The purpose of the study is to evaluate the efficacy, tolerability, and safety of vigabatrin versus rapamycin as a preventive treatment in infants with Tuberous Sclerosis Complex (TSC).
Phase:
Phase 2/Phase 3
Details
Lead Sponsor:
Katarzyna Kotulska
Treatments:
Sirolimus
Vigabatrin