Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I
Status:
Terminated
Trial end date:
2020-10-01
Target enrollment:
Participant gender:
Summary
This is a five-year extension study of the pilot study, "Intrathecal Enzyme Replacement for
Cognitive Decline in MPS I". Participants must have completed the pilot study to participate
in this study.
Phase:
N/A
Details
Lead Sponsor:
agnes chen
Collaborators:
Children's Hospital & Research Center Oakland National Institute of Neurological Disorders and Stroke (NINDS) Rare Diseases Clinical Research Network The Ryan Foundation UCSF Benioff Children's Hospital Oakland University of California, Los Angeles University of Minnesota University of Minnesota - Clinical and Translational Science Institute