Overview

Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B

Status:
Recruiting
Trial end date:
2026-12-01
Target enrollment:
Participant gender:
Summary
Primary Objective: - To confirm appropriate dose levels of fitusiran when administered to male pediatric participants (ages 1 to <12 years of age) with severe hemophilia A or B Secondary Objective: - To characterize the safety and tolerability - To determine fitusiran plasma concentrations at selected time points
Phase:
Phase 2/Phase 3
Details
Lead Sponsor:
Genzyme, a Sanofi Company
Treatments:
Factor VIII