GlycoCholic Acid Treatment for Patients With Inborn Errors in Bile Acid Synthesis
Status:
Unknown status
Trial end date:
2020-12-01
Target enrollment:
Participant gender:
Summary
The purpose of this research study is to determine the way (mechanisms) by which your defect
in bile acid handling (metabolism) causes your liver disease or abnormality in absorption of
vitamins and the effect of an investigational bile acid therapy (glycocholic acid) on your
vitamin absorption and your liver disease. An investigational therapy is one that not
approved by the United States Food and Drug Administration (FDA) and is being provided to you
under an Investigational New Drug application from the FDA.
Phase:
Phase 3
Details
Lead Sponsor:
Children's Hospital Medical Center, Cincinnati
Treatments:
Bile Acids and Salts Cholic Acids Glycocholic Acid