Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism
Status:
Terminated
Trial end date:
2010-02-01
Target enrollment:
Participant gender:
Summary
The primary objective of this clinical trial is to evaluate the ability to achieve and
sustain donor engraftment in patients with lysosomal and peroxisomal inborn errors of
metabolism undergoing hematopoietic stem cell transplantation (HCT).