Hematopoietic Stem Cell Transplantation for Malignant Infantile Osteopetrosis
Status:
Unknown status
Trial end date:
2012-12-01
Target enrollment:
Participant gender:
Summary
The purpose of this study is to evaluate the efficacy and side effects of donor hematopoietic
cells using chemotherapy regimen without total-body irradiation in children undergoing a
hematopoietic stem cell transplant for Malignant infantile osteopetrosis. The blood stem
cells will be derived from either related donor or unrelated umbilical cord blood or
haploidentical donor.