Overview

In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases

Status:
Recruiting
Trial end date:
2032-04-01
Target enrollment:
Participant gender:
Summary
The investigators aims to determine the the maternal and fetal safety and feasibility of in utero fetal enzyme replacement therapy in fetuses with Lysosomal Storage Diseases.
Phase:
Phase 1
Details
Lead Sponsor:
University of California, San Francisco
Collaborator:
Duke University