Overview

Long-term Evaluation on Height and Weight in Patients With MPS II Who Started Treatment at < 6 Years of Age

Status:
Active, not recruiting
Trial end date:
2025-07-09
Target enrollment:
Participant gender:
Summary
This long-term study will provide Elaprase treatment to children enrolled in this study and will utilize data from both enrolled patients and Hunter Outcome Survey (HOS) patient registry data to conduct the primary growth analysis to assess changes in height and weight in patients with Mucopolysaccharidosis II (Hunter syndrome) MPS II.
Phase:
Phase 4
Details
Lead Sponsor:
Shire