Low Dose Treosulfan Based Conditioning Regimen and PTCy in HSCT for Nijmegen Breakage Syndrome
Status:
Recruiting
Trial end date:
2029-01-31
Target enrollment:
Participant gender:
Summary
The aim of the current study is to evaluate the safety and efficacy of low dose treosulfan
based conditioning regimen in HSCT with post-transplant cyclophosphamide in Nijmegen breakage
syndrome
Phase:
Phase 2
Details
Lead Sponsor:
Federal Research Institute of Pediatric Hematology, Oncology and Immunology