Overview

NAD Supplementation to Prevent Progressive Neurological Disease in Ataxia Telangiectasia

Status:
Active, not recruiting
Trial end date:
2027-02-16
Target enrollment:
Participant gender:
Summary
The study investigates the effect of dietary supplementation of nicotinamide ribonucleoside (NR) in children with ataxia telangiectasia (AT), with main focus on neurological symptoms.
Phase:
Phase 2
Details
Lead Sponsor:
University Hospital, Akershus
Collaborators:
Haukeland University Hospital
Oslo University Hospital
South-Eastern Norway Regional Health Authority
St. Olavs Hospital
Sykehuset Innlandet HF
The Bergesen Foundation
University Hospital of North Norway
University of Bergen
Treatments:
Niacin
Niacinamide
Nicotinic Acids