Neuroimaging and Neurocognitive Assessment and Response to Sapropterin Dihydrochloride Treatment in Phenylketonuria
Status:
Withdrawn
Trial end date:
2012-12-01
Target enrollment:
Participant gender:
Summary
The investigators will use different types of brain imaging (MRI) in patients with
Phenylketonuria (PKU) who are currently not on a strict diet to test the hypothesis that
there is improvement in brain circuitry and biochemistry after return to diet and/or
sapropterin dihydrochloride (Kuvan).
Phase:
N/A
Details
Lead Sponsor:
Children's National Research Institute Children's Research Institute