Once-A-Day Prophylaxis for Youth and Young Adults With Severe Hemophilia A
Status:
Completed
Trial end date:
2011-04-01
Target enrollment:
Participant gender:
Summary
The primary objective of this study is to test the feasibility of a large-scale clinical
trial of once-daily prophylaxis. The secondary objectives are to collect clinical efficacy
outcomes so that we can better plan a large-scale study; we will estimate the effect size and
variability of effect and resource utilization of once-daily prophylaxis to allow us to set a
sample size for a definitive trial.