Overview

RPE65 Gene Therapy (LX101)for Leber's Congenital Amaurosis

Status:
Not yet recruiting
Trial end date:
2023-06-01
Target enrollment:
Participant gender:
Summary
The purpose of this study is to determine whether gene transfer(LX101) will be safe and effective in the treatment of Leber Congenital Amaurosis (LCA).
Phase:
N/A
Details
Lead Sponsor:
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine