Overview

Response to Phenylketonuria to Tetrahydrobiopterin (BH4)

Status:
Terminated
Trial end date:
2015-01-01
Target enrollment:
Participant gender:
Summary
The purpose of this study is to determine whether tetrahydrobiopterin (BH4)is effective in treating patients with PKU.
Phase:
Phase 1
Details
Lead Sponsor:
FDA Office of Orphan Products Development
The University of Texas Medical Branch, Galveston