Overview

Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of SPG302 in Healthy Volunteers and ALS Participants

Status:
Not yet recruiting
Trial end date:
2024-12-01
Target enrollment:
0
Participant gender:
All
Summary
The first-in-human Phase 1 study described herein will evaluate the safety, tolerability, pharmacokinetics and pharmacodynamics of SPG302 in healthy volunteers and ALS participants
Phase:
Phase 1
Accepts Healthy Volunteers?
Accepts Healthy Volunteers
Details
Lead Sponsor:
Spinogenix
Criteria
Inclusion Criteria:

- Age 18-55

- Must be in good health with no significant medical history

- Clinical laboratory values within normal range

- BMI 18-32 (inclusive)

- Contraceptive use by men or women consistent with local regulations

- Able and willing to provide written informed consent

Exclusion Criteria:

- Any physical or psychological condition that prohibits study completion

- Known cardiac disease

- Active or history of malignancy in the past 5 years

- Serious infection within 1 month of screening

- Acute illness within 30 days of Day 1

- Surgery, bone fracture, or major musculoskeletal injury in the past 3 months

- History of suicidal behavior or suicidal ideation

- Active cigarette smokers and users of nicotine-containing products

- HIV, hepatitis B and hepatitis C positive

- SBP >140 or <90

- DBP >90 or <40

- HR <40 or >100

- QTcF >450ms, cardiac arrhythmia, or clinically significant abnormal ECG

- Prescriptions, over-the-counter, or herbal medication within 7 days

- Vaccines within 14 days

- Other investigational products within 30 days

- Blood donation within 30 days

- Plasma donation within 7 days

- Pregnant or breastfeeding

- Otherwise unfit, on metabolic-altering lifestyle/diet, positive urine drug screen or
intake of alcohol or caffeine-containing products

ALS Cohort Inclusion Criteria:

- Age 18-80

- ALS

- FVC>80%

- ALSFRS-R >=12 points

- Stable dose of standard of care treatment

- Contraception use by men or women consistent with local regulations

- Able and willing to provide written informed consent

ALS Cohort Exclusion Criteria:

- Underlying physical or psychological condition prohibiting study completion

- Known cardiac disease

- Active or history of malignancy in the past 5 years

- Serious infection within 1 month of screening

- Acute illness within 30 days of Day 1

- Surgery, bone fracture, or major musculoskeletal injury in the past 3 months

- History of suicidal behavior or suicidal ideation

- Active cigarette smokers and users of nicotine-containing products

- Neurodegenerative disease

- External respiratory support or supplemental oxygen requirement

- HIV, hepatitis B and hepatitis C positive

- SBP >140 or <90

- DBP >90 or <40

- HR <40 or >100

- QTcF >450ms, cardiac arrhythmia, or clinically significant abnormal ECG

- Vaccines within 14 days

- Other investigational products within 30 days

- Blood donation within 30 days

- Plasma donation within 7 days

- Pregnant or breastfeeding

- Otherwise unfit