Overview

Sirolimus for Leigh Syndrome

Status:
ENROLLING_BY_INVITATION
Trial end date:
2027-12-01
Target enrollment:
Participant gender:
Summary
The purpose of this study is to evaluate the safety and efficacy of the drug Sirolimus in participants with Leigh syndrome.
Phase:
PHASE2
Details
Lead Sponsor:
Matthew Demczko
Treatments:
Sirolimus