Overview

Study of Eteplirsen in DMD Patients

Status:
Completed
Trial end date:
2019-06-14
Target enrollment:
Participant gender:
Summary
The main objective of this study is to provide evidence of efficacy of eteplirsen (AVI-4658) in Duchenne muscular dystrophy (DMD) patients that are amenable to skipping exon 51. Additional objectives include evaluation of safety, biomarkers and the long-term effects of eteplirsen up to 96 weeks, followed by a safety extension (not to exceed 48 weeks).
Phase:
Phase 3
Details
Lead Sponsor:
Sarepta Therapeutics
Sarepta Therapeutics, Inc.