Overview

Study of ORL-1G (D-galactose) in Patients With Glycogen Storage Disease Type 14

Status:
Unknown status
Trial end date:
2019-10-31
Target enrollment:
0
Participant gender:
All
Summary
Study of ORL-1G in Patients With Glycogen Storage Disease Type 14
Phase:
Phase 1/Phase 2
Accepts Healthy Volunteers?
No
Details
Lead Sponsor:
Orpha Labs
Criteria
Inclusion Criteria:

- Diagnosis of Glycogen Storage Disease Type 14.

- Less than 18 years old.

Exclusion Criteria:

- Diagnosis of any other disease that is not a manifestation of Glycogen Storage Disease
Type 14.