This is a phase 1 / 2, randomized, double-blinded, single cross-over study, with a washout
period between treatment regimens, to test the efficacy and safety of tamoxifen therapy to
improve motor and respiratory function in males with XLMTM.
Phase:
Phase 1/Phase 2
Details
Lead Sponsor:
James Dowling
Collaborators:
Canadian Institutes of Health Research (CIHR) Cures Within Reach Great Ormond Street Hospital Charity Mogford Campbell Family Chair Fund Myotubular Trust Sparks The Joshua Frase Foundation USA Will Cure USA