Overview

Triheptanoin Treatment Trial for Patients With Adult Polyglucosan Body Disease

Status:
Completed
Trial end date:
2015-07-01
Target enrollment:
Participant gender:
Summary
The purpose of the study is to determine if triheptanoin is an effective treatment for the symptoms of Adult Polyglucosan Body Disease.
Phase:
Phase 2
Details
Lead Sponsor:
Baylor Research Institute
Collaborator:
Ultragenyx Pharmaceutical Inc