This study is a pilot, open-label, single-arm study to evaluate the effect of the sickle cell
medication voxelotor on exercise capacity, as measured by cardiopulmonary exercise testing
(CPET) in patients 12 years of age and older with sickle cell anemia (SCA).
Phase:
Phase 4
Details
Lead Sponsor:
Elizabeth Yang Elizabeth Yang, MD, PhD
Collaborators:
Global Blood Therapeutics Mednax Center for Research, Education, Quality and Safety University of California, San Francisco