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Clinical Trials for Wolfram Syndrome

  • A Phase II Study of Safety and Efficacy of AMX0035 in Adult Patients With Wolfram Syndrome
  • Tirzepatide Monotherapy in Patients With Wolfram Syndrome Type 1
  • Efficacy Study of Daily Administration of VPA in Patients Affected by Wolfram Syndrome
  • Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome
  • Treatment of Wolfram Syndrome Type 2 With the Chelator Deferiprone and Incretin Based Therapy
  • A Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome
  • GLP Analogs for Diabetes in Wolfram Syndrome Patients
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