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Clinical Trials for Mucopolysaccharidosis II

• An Extension Study of the Long-Term Safety, Tolerability, and Efficacy of Tividenofusp Alfa (DNL310) in Participants With Mucopolysaccharidosis Type II (MPS II) From Study DNLI-E-0002 or Study DNLI-E-0007
• Extension Study of Idursulfase-IT Along With Elaprase in Children and Adults With Hunter Syndrome and Cognitive Impairment
• An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in Mucopolysaccharidosis Type II (Hunter Syndrome) Male Subjects
• A Study of ELAPRASE in Treatment-naïve Participants With Hunter Syndrome (Mucopolysaccharidosis [MPS] II)
• A Study to the Efficacy and Safety of DNL310 vs Idursulfase in Pediatric Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
• A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
• A Phase Ⅲ Study of JR-141 in Patients With Mucopolysaccharidosis II
• An Extension Study of JR-141 in Patients With Mucopolysaccharidosis II
• A Study of DNL310 in Pediatric Participants With Hunter Syndrome
• An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis II
• A Study of JR-141 in Patients With Mucopolysaccharidosis II
• A Study of JR-141 in Patients With Mucopolysaccharidosis II
• Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II
• A Study of JR-141 in Patients With Mucopolysaccharidosis Type II
• Long-term Evaluation on Height and Weight in Patients With MPS II Who Started Treatment at < 6 Years of Age
• Effects of Adalimumab in Mucopolysaccharidosis Types I, II and VI
• Study of Long Term Safety and Clinical Outcomes of Idursulfase IT and Elaprase Treatment in Pediatric Participants Who Have Completed Study HGT-HIT-094
• MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
• A Study to Test the Possibility of Cross Reaction Induced by the Idursulfase Drug to GSK2788723
• Extension Study of HGT-HIT-045 Evaluating Long-Term Safety and Clinical Outcomes of Idursulfase-IT in Conjunction With Elaprase in Pediatric Participants With Hunter Syndrome and Cognitive Impairment
• To Evaluate the Safety and Efficacy of GC1111 (Recombinant Human Iduronate-2-sulfatase) in Hunter Syndrome Patients
• Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders
• A Safety and Dose Ranging Study of Idursulfase (Intrathecal) Administration Via an Intrathecal Drug Delivery Device in Pediatric Patients With Hunter Syndrome Who Have Central Nervous System Involvement and Are Receiving Treatment With Elaprase®
• Clinical Trial of Growth Hormone in MPS I, II, and VI